Gene Therapy for Hemophilia: A Breakthrough Treatment

April 18, 2025

Gene therapy for hemophilia is revolutionizing the landscape of hemophilia treatment, offering hope to patients who have long relied on daily injections of clotting factor.One groundbreaking example is the recent FDA-approved therapy called Hemgenix, designed specifically for hemophilia B, which significantly increases levels of clotting factor IX in the bloodstream.
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